Ionis Pharmaceuticals

Ionis Pharmaceuticals, Inc. is a biotechnology company based in Carlsbad, California, that specializes in discovering and developing RNA-targeted therapeutics. The company has three commercially approved medicines: Spinraza (Nusinersen), Tegsedi (Inotersen), and Waylivra (Volanesorsen) and has four drugs in pivotal studies: tominersen for Huntington's disease, tofersen for SOD1-ALS, AKCEA-APO(a)-LRx for cardiovascular disease, and AKCEA-TTR-LRx for all forms of TTR amyloidosis.

Ionis Pharmaceuticals, Inc.
FormerlyIsis Pharmaceuticals, Inc.
Company typePublic company
Traded as
  • Nasdaq: IONS
  • Russell 1000 component
IndustryBiotechnology
Founded1989 (1989)
FounderStanley T. Crooke
HeadquartersCarlsbad, California, U.S.
Key people
Brett P. Monia (CEO)
Elizabeth L. Hougen (CFO)
Joseph Loscalzo
(Chairman of the Board)
Productsnusinersen, inotersen, volanesorsen, plazomicin, mipomersen
Revenue US$587 million (2022)
Net income
US$−270 million (2022)
Total assets US$2.53 billion (2022)
Total equity US$573 million (2022)
Number of employees
796 (December 2022)
Websiteionispharma.com
Footnotes / references

The company was named Isis Pharmaceuticals until December 2015.

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